Defects in PRF1 are a cause of familial hemophagocytic lymphohistiocytosis type 2, a rare and lethal autosomal recessive disorder of early childhood characterized by excessive immune activation. Patients have a nonmalignant accumulation and multivisceral infiltration of activated T lymphocytes and histiocytes (macrophages).
Alternative names
FHL2
HPLH2, HLH
Familial erythrophagocytic lymphohistiocytosis 2
Familial histiocytic reticulosis 2
Hemophagocytic lymphohistiocytosis
Classification
- Defects of phagocyte function
- Familial haemophagocytic lymphohistiocytosis
- Familial haemophagocytic lymphohistiocytosis type 2
- Familial haemophagocytic lymphohistiocytosis
Inheritance
Autosomal recessive
Cross references
Phenotypically related immunodeficiencies
Incidence
1:50,000 births