Combined B and T cell immunodeficiencies |
T-B- Severe combined immunodeficiency (SCID) |
Disease
|
Fact file |
Gene |
Structures |
Reticular dysgenesis |
1 |
|
|
RAG1 deficiency |
2 |
RAG1 |
PDB: 1RMD |
RAG2 deficiency |
3 |
RAG2 |
|
Omenn syndrome |
4 |
RAG1 |
PDB: 1RMD |
Artemis deficiency |
5 |
DCLRE1C |
|
T-B+ SCID |
Disease
|
Fact file |
Gene |
Structures |
X-linked SCID(γc-chain deficiency) |
8 |
IL2RG |
|
JAK3 deficiency |
9 |
JAK3 |
|
Interleukin 7 receptor deficiency |
106 |
IL7R |
|
CD45 deficiency |
6 |
PTPRC |
|
CD3delta deficiency |
111 |
CD3D |
|
T-cell immunodeficiency, congenital alopecia, and nail dystrophy |
128 |
FOXN1 |
|
Deficiencies of purine metabolism |
Disease
|
Fact file |
Gene |
Structures |
Adenosine deaminase deficiency |
10 |
ADA |
|
Purine nucleoside phosphorylase deficiency |
11 |
NP |
PDB: 1ULA, PDB: 1ULB
|
Major histocompatibility complex class II deficiency |
Disease
|
Fact file |
Gene |
Structures |
CIITA, MHCII transactivating protein deficiency |
12 |
CIITA |
|
RFX-5, MHCII promoter X box regulatory factor 5 deficiency |
13 |
RFX5 |
|
Regulatory factor X-associated protein deficiency |
14 |
RFXAP |
|
RFXANK, Ankyrin repeat containing regulatory factor X-associated protein deficiency |
15 |
RFXANK |
|
Major histocompatibility complex class I deficiency |
Disease
|
Fact file |
Gene |
Structures |
TAP2 deficiency |
60 |
TAP2 |
|
TAP1 deficiency |
107 |
TAP1 |
PDB: 1JJ7 |
Tapasin deficiency |
136 |
TAPBP |
|
Hyper-IgM syndrome |
Disease
|
Fact file |
Gene |
Structures |
X-linked hyper-IgM syndrome (CD40L deficiency) |
16 |
TNFSF5 |
PDB: 1ALY, PDB: 1CDA
|
CD40 deficiency |
18 |
CD40 |
PDB: 1CDF |
CD3 deficiency |
Disease
|
Fact file |
Gene |
Structures |
CD3ε deficiency |
20 |
CD3E |
|
CD3γ deficiency |
21 |
CD3G |
|
CD3Zeta deficiency |
149 |
CD247 |
PDB: 1TCE |
Other |
Disease
|
Fact file |
Gene |
Structures |
ZAP-70 deficiency |
62 |
ZAP70 |
|
IL-2 receptor α-chain deficiency (CD25 deficiency) |
63 |
IL2RA |
PDB: 1ILM, PDB: 1ILN
|
CD8α deficiency |
64 |
CD8A |
PDB: 1CD8 |
p56 Lck deficiency |
137 |
LCK |
PDB: 1BHF, PDB: 1BHH, PDB: 1CWD, PDB: 1CWE, PDB: 1FBZ, PDB: 1H92, PDB: 1IJR, PDB: 1KIK, PDB: 1LCJ, PDB: 1LCK, PDB: 1LKK, PDB: 1LKL, PDB: 1Q68, PDB: 1Q69, PDB: 1QPC, PDB: 1QPD, PDB: 1QPE, PDB: 1QPJ, PDB: 3LCK
|
Schimke immuno-osseous dysplasia |
148 |
SMARCAL1 |
|
Cernunnos deficiency |
152 |
NHEJ1 |
|
TMEM142 deficiency |
147 |
ORAI1 |
|
Deficiencies predominantly affecting antibody production |
Agammaglobulinemia |
Disease
|
Fact file |
Gene |
Structures |
X-linked agammaglobulinemia |
22 |
BTK |
PDB: 1BTK, PDB: 1AWW, PDB: 1AWX, PDB: 1B55, PDB: 1BWN, PDB: 1K2P
|
X-linked hypogammaglobulinemia with growth hormone deficiency |
23 |
|
|
BLNK deficiency |
24 |
BLNK |
|
Igα deficiency |
25 |
CD79A |
|
μ heavy-chain deficiency |
26 |
IGHM |
|
λ5 surrogate light-chain deficiency |
27 |
IGLL1 |
|
Non-Bruton type autosomal dominant agammaglobulinemia |
151 |
LRRC8A |
|
Igβ deficiency |
159 |
CD79B |
|
Light-chain deficiency |
Disease
|
Fact file |
Gene |
Structures |
κ light-chain deficiency |
65 |
IGKC |
|
Selective deficiency of IgG subclass, IgE and/or IgA class or subclass |
Disease
|
Fact file |
Gene |
Structures |
γ1 isotype deficiency |
28 |
IGHG1 |
PDB: 1FC1, PDB: 1FC2
|
γ2 isotype deficiency |
29 |
IGHG2 |
|
Partial γ3 isotype deficiency |
30 |
IGHG3 |
|
γ4 isotype deficiency |
31 |
IGHG4 |
|
α1 isotype deficiency |
32 |
IGHA1 |
|
α2 isotype deficiency |
33 |
IGHA2 |
|
ε isotype deficiency |
34 |
IGHE |
PDB: 1IGE |
IgG subclass deficiency with or without IgA deficiency |
35 |
|
|
IgA deficiency |
67 |
IGAD1 |
|
Common variable immunodeficiency |
Disease
|
Fact file |
Gene |
Structures |
Common variable immunodeficiency of unknown origin |
66 |
|
|
ICOS deficiency |
116 |
ICOS |
|
TNFRSF13B deficiency |
153 |
TNFRSF13B |
PDB: 1XU1, PDB: 1XUT
|
Other antibody deficiencies |
Disease
|
Fact file |
Gene |
Structures |
Antibody deficiency with normal immunoglobulin levels |
68 |
|
|
Transient hypogammaglobulinemia of infancy |
69 |
|
|
CD19 deficiency |
150 |
CD19 |
|
Defects of class-switch recombination and somatic hypermutation (Hyper-IgM syndromes) affecting B cells |
Disease
|
Fact file |
Gene |
Structures |
AID deficiency |
17 |
AICDA |
|
UNG deficiency |
127 |
UNG |
PDB: 1AKZ, PDB: 1EMH, PDB: 1EMJ, PDB: 1SSP, PDB: 1UGH, PDB: 2SSP, PDB: 4SKN
|
Selective deficiency in Ig class-switch recombination |
138 |
|
|
Defects in lymphocyte apoptosis |
Autoimmune lymphoproliferative syndrome |
Disease
|
Fact file |
Gene |
Structures |
Autoimmune lymphoproliferative syndrome, type Ia |
36 |
TNFRSF6 |
PDB: 1DDF |
Autoimmune lymphoproliferative syndrome, type 1B |
37 |
FASLG |
|
Autoimmune lymphoproliferative syndrome type II |
109 |
CASP10 |
|
Autoimmune lymphoproliferative syndrome type IIB |
110 |
CASP8 |
PDB: 1F9E, PDB: 1QDU, PDB: 1QTN
|
ALPS type III |
162 |
NRAS |
|
Other well-defined immunodeficiency syndromes |
Wiskott-Aldrich syndrome and X-linked thrombocytopenia | 71 |
WAS |
|
Autoimmune disorders |
Disease
|
Fact file |
Gene |
Structures |
Autoimmune polyendocrinopathy with candidiasis and ectodermal dystrophy |
72 |
AIRE |
|
X-linked immunodeficiency, polyendocrinopathy, enteropathy(IPEX) |
78 |
FOXP3 |
|
X-linked lymphoproliferative disease (Duncan disease) | 73 |
SH2D1A |
PDB: 1D1Z |
DiGeorge-anomaly | 74 |
DGCR |
|
Hyper-IgE recurrent infection syndrome | 75 |
TYK2 |
|
Chronic mucocutaneous candidiasis | 76 |
|
|
Cartilage-hair hypoplasia | 77 |
RMRP |
|
Epidermodysplasia verruciformis |
Disease
|
Fact file |
Gene |
Structures |
Epidermodysplasia verruciformis type 1 |
114 |
TMC6 |
|
Epidermodysplasia verruciformis type 2 |
115 |
TMC8 |
|
Netherton syndrome | 133 |
SPINK5 |
PDB: 1H0Z, PDB: 1HDL
|
Natural killer deficiency | 135 |
FCGR3A |
|
Transcobalamin II deficiency | 130 |
TCN2 |
|
Osteopetrosis, AR | 157 |
TCIRG1 |
|
Hepatic veno-oclussive disease with immunodeficiency syndrome | 158 |
SP110 |
|
Tyk2 deficiency | 163 |
TYK2 |
|
X-linked lymphoproliferative syndrome 2 | 165 |
BIRC4 |
PDB: 1C9Q, PDB: 1F9X, PDB: 1G3F, PDB: 1G73, PDB: 1I3O, PDB: 1I4O, PDB: 1I51, PDB: 1KMC, PDB: 1NW9, PDB: 1TFQ
|
STAT3 deficiency | 167 |
STAT3 |
|
Defects of phagocyte function |
Chronic granulomatous disease |
Disease
|
Fact file |
Gene |
Structures |
X-linked chronic granulomatous disease |
38 |
CYBB |
|
p22phox deficiency |
39 |
CYBA |
|
p47phox deficiency |
40 |
NCF1 |
PDB: 1GD5 |
p67phox deficiency |
41 |
NCF2 |
PDB: 1E96 |
Leukocyte adhesion defects |
Disease
|
Fact file |
Gene |
Structures |
Leukocyte adhesion deficiency I |
42 |
ITGB2 |
|
Leukocyte adhesion deficiency II |
43 |
SLC35C1 |
|
LAD3 deficiency |
139 |
RASGRP2 |
|
LAD with RAC2 deficiency |
123 |
RAC2 |
PDB: 1DS6 |
Chediak-Higashi syndrome | 79 |
LYST |
|
Griscelli syndrome |
Disease
|
Fact file |
Gene |
Structures |
Griscelli syndrome, type 1 |
80 |
MYO5A |
|
Griscelli syndrome, type 2 |
122 |
RAB27A |
|
Griscelli syndrome, type 3 |
156 |
MLPH |
|
Glucose 6-phosphate dehydrogenase deficiency | 81 |
G6PD |
|
Myeloperoxidase deficiency | 82 |
MPO |
PDB: 1MHL, PDB: 1CXP, PDB: 1D2V, PDB: 1D5L, PDB: 1D7W, PDB: 1DNU, PDB: 1DNW
|
Glycogen storage disease Ib | 83 |
G6PC |
|
Shwachman syndrome | 84 |
SBDS |
|
Neutropenia |
Disease
|
Fact file |
Gene |
Structures |
Severe congenital neutropenias, including Kostmann syndrome |
85 |
CSF3R |
PDB: 1AZ7 |
Cyclic neutropenia |
86 |
ELA2 |
PDB: 1HNE, PDB: 1PPF, PDB: 1PPG, PDB: 1B0F
|
GFI1 deficiency |
129 |
GFI1 |
|
Familial haemophagocytic lymphohistiocytosis |
Disease
|
Fact file |
Gene |
Structures |
Familial haemophagocytic lymphohistiocytosis type 1 |
104 |
|
|
Familial haemophagocytic lymphohistiocytosis type 2 |
105 |
PRF1 |
|
Familial hemophagocytic lymphohistiocytosis 3 |
126 |
UNC13D |
|
Familial haemophagocytic lymphohistiocytosis type 4 |
155 |
STX11 |
|
Hoyeraal-Hreidarsson syndrome/Dyskeratosis congenita | 113 |
DKC1 |
|
CD64 deficiency | 132 |
FCGR1A |
|
Hermansky-Pudlak syndrome 2 | 108 |
AP3B1 |
|
Barth syndrome | 134 |
TAZ |
|
Neutrophil-specific granule deficiency | 112 |
CEBPE |
|
Papillon-Lefevre syndrome | 154 |
CTSC |
PDB: 1K3B |
Disorders of pigmentation and immunodeficiency |
Disease
|
Fact file |
Gene |
Structures |
p14 deficiency |
161 |
MAPBPIP |
|
Defects of innate immune system, receptors and signaling components |
Interferon-γ (IFNγ) receptor deficiency |
Disease
|
Fact file |
Gene |
Structures |
IFNγ1-receptor deficiency |
44 |
IFNGR1 |
PDB: 1JRH, PDB: 1FG9
|
IFNγ2-receptor deficiency |
45 |
IFNGR2 |
|
Interleukin-12 receptor β1 deficiency | 47 |
IL12RB1 |
|
Interleukin-12 (IL-12) p40 deficiency | 46 |
IL12B |
|
STAT1 deficiency | 70 |
STAT1 |
PDB: 1BF5 |
STAT5b deficiency | 125 |
STAT5B |
|
IRAK4 deficiency | 117 |
IRAK4 |
|
Autosomal dominant anhidrotic ectodermal dysplasia and T-cell immunodeficiency | 121 |
NFKBIA |
|
WHIM syndrome | 7 |
CXCR4 |
|
X-linked hyper-IgM syndrome and hypohydrotic ectodermal dysplasia (Nemo deficiency) | 19 |
IKBKG |
|
UNC93B deficiency | 164 |
UNC93B1 |
|
TLR3 deficiency | 166 |
TLR3 |
PDB: 1ZIW, PDB: 2A0Z
|
DNA breakage associated syndromes and DNA epigenetic modification syndromes |
DNA-breakage-associated syndromes |
Disease
|
Fact file |
Gene |
Structures |
Ataxia-telengiectasia |
87 |
ATM |
|
Nijmegen-breakage syndrome |
88 |
NBS1 |
|
Ataxia-telangiectasia-like disorder |
120 |
MRE11A |
|
DNA ligase deficiency |
Disease
|
Fact file |
Gene |
Structures |
DNA ligase I deficiency |
131 |
LIG1 |
|
DNA ligase deficiency IV |
118 |
LIG4 |
PDB: 1IK9 |
Bloom syndrome | 89 |
BLM |
|
Immunodeficiency, centromere instability and facial abnormalities syndrome (ICF) | 124 |
DNMT3B |
|
Defects of the classical complement cascade proteins |
C1q deficiency |
Disease
|
Fact file |
Gene |
Structures |
C1q α-polypeptide deficiency |
48 |
C1QA |
|
C1q β-polypeptide deficiency |
49 |
C1QB |
|
C1q γ-polypeptide deficiency |
50 |
C1QC |
|
C1r and C1s deficiency |
Disease
|
Fact file |
Gene |
Structures |
C1r deficiency |
51 |
C1R |
PDB: 1APQ |
C1s deficiency |
52 |
C1S |
|
C2 deficiency | 90 |
C2 |
|
C3 deficiency | 61 |
C3 |
PDB: 1C3D |
C4 deficiency |
Disease
|
Fact file |
Gene |
Structures |
C4A deficiency |
53 |
C4A |
|
C4B deficiency |
54 |
C4B |
|
C5 deficiency | 91 |
C5 |
PDB: 1KJS, PDB: 1CFA
|
C6 deficiency | 92 |
C6 |
|
C7 deficiency | 93 |
C7 |
|
C8 deficiency |
Disease
|
Fact file |
Gene |
Structures |
C8 α-polypeptide deficiency |
55 |
C8A |
|
C8 β-polypeptide deficiency |
56 |
C8B |
|
C8 γ-polypeptide deficiency |
57 |
C8G |
|
C9 deficiency | 94 |
C9 |
|
Defects of the alternative complement pathway |
Factor B deficiency | 95 |
BF |
|
Factor D deficiency | 98 |
CFD |
PDB: 1DFP, PDB: 1DST, PDB: 1DSU
|
Factor H1 deficiency | 101 |
CFH |
PDB: 1HCC, PDB: 1HFH, PDB: 1HFI
|
Properdin factor C deficiency | 100 |
CFP |
|
Defects of complement regulatory proteins |
Hereditary angioedema |
Disease
|
Fact file |
Gene |
Structures |
Hereditary angioedema |
97 |
SERPING1 |
|
C4-binding protein deficiency |
Disease
|
Fact file |
Gene |
Structures |
C4 binding protein α deficiency |
58 |
C4BPA |
|
C4 binding protein β deficiency |
59 |
C4BPB |
|
Hereditary angioedema type III |
160 |
F12 |
|
Decay-accelerating factor (CD55) deficiency | 102 |
CD55 |
|
Factor I deficiency | 99 |
CFI |
|
MAC inhibitor (CD59) deficiency | 103 |
CD59 |
PDB: 1CDQ, PDB: 1CDR, PDB: 1CDS, PDB: 1ERG, PDB: 1ERH
|
Mannose-binding lectin deficiency |
Disease
|
Fact file |
Gene |
Structures |
Mannose-binding lectin deficiency |
96 |
MBL2 |
PDB: 1HUP |
Mannan-binding lectin - associated serine protease 2 deficiency |
119 |
MASP2 |
|
Periodic fever syndromes |
Familial mediterranean fever | 140 |
MEFV |
|
Hyperimmunoglobulinemia D with periodic fever syndrome | 141 |
MVK |
|
Tumor necrosis factor receptor-associated periodic syndrome | 142 |
TNFRSF1A |
PDB: 1EXT, PDB: 1FT4, PDB: 1ICH, PDB: 1NCF, PDB: 1TNR
|
Cold autoinflammatory syndrome |
Disease
|
Fact file |
Gene |
Structures |
Familial cold urticaria and Muckle-Wells syndrome |
143 |
CIAS1 |
|
Chronic infantile neurological cutaneous and articular syndrome |
144 |
CIAS1 |
|
Granulomatous sinovitis with uveitis and cranial neuropathies | 145 |
CARD15 |
|
Crohn's disease | 146 |
CARD15 |
|