In glycogen storage disease type I, the enzyme glucose-6-phosphatase is defective in the liver, kidney, and small intestine, where it normally functions. Type Ia represent the true enzymatic defect, and type Ib represent the transport defect. GSD Ia and Ib are autosomal recessive genetic traits. Although extremely rare there are patients with subtypes Ic and Id, probably due to unusual mutations in the translocase gene (11q23).
Alternative names
GSD1B
Glucose-6-phosphatase transport defect
Classification
- Defects of phagocyte function
Inheritance
Autosomal recessive